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Brineura - CLN2 treatment (Lily Rumph) View |
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The Race for Brineura (Trailer) (Brineura™ (cerliponase alfa)) View |
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CLN2 Batten Disease - Jessica's Brinuera Journey showing what early access to treatment can do (Gail Rich) View |
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Brief video describing CLN2 Enzyme replacement therapy and research (Diane-Marie Brache) View |
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Cln 2 brineura boala batten (Rebeca faith-hope-love) View |
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Brineura (Anna) View |
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Treatment for CLN2 Batten Disease (Ollie's Army Battling Against Battens) View |
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Leqselvi for Alopecia Areata, Femlyv Dissolvable Birth Control, Brineura for Batten Disease,... (Nascent Medical) View |
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Ultragenyx Ventures into Gene Therapy for Wilson Disease (Wilson Disease Association) View |
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Isabel, 9, has infantile Batten disease. Mum Sophie talks about their journey so far #battenstories (Batten Disease Family Association) View |