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Real-Life Outcome Data With Risdiplam for Spinal Muscular Atrophy (CheckRare) View |
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Risdiplam: An Oral Treatment for Spinal Muscular Atrophy (NeurologyLive) View |
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Positive Safety and Efficacy Data for Intrathecal Administration of Gene Therapy for SMA (CheckRare) View |
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1st Year Evrysdi Update: My experience a year in. (My Big Full Authentic Life with LaMondre) View |
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Risdiplam Under Study to Treat SMA (NeurologyLive) View |
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My Risdiplam / Evrysdi Journey Day 02 (The SMArt Chap) View |
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Four Clinical Trials Testing Risdiplam Across Various SMA Subtypes (CheckRare) View |
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Scholar Rock - Spinal Muscular Atrophy (SMA) Trials (HPR) View |
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Risdiplam Day 25 (The SMArt Chap) View |
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Stander Use in Spinal Muscular Atrophy: Results From a Large Natural History Database (Pediatric Physical Therapy Journal) View |